ACTIVE_NOT_RECRUITING

RGX-314 Gene Therapy Administered in the Suprachoroidal Space for Participants With Diabetic Retinopathy (DR) With and Without Center Involved-Diabetic Macular Edema (CI-DME)

Study Overview

This clinical trial focuses on testing the efficacy of different digital interventions to promote re-engagement in cancer-related long-term follow-up care for adolescent and young adult (AYA) survivors of childhood cancer.

Description

ABBV-RGX-314 is being developed as a novel, potential one-time gene therapy treatment for the treatment of Diabetic Retinopathy (DR) with and without Center-Involved Diabetic Macular Edema (CI-DME). DR is a chronic and progressive complication of diabetes mellitus. It is a sight-threatening disease characterized in the early stages by neuronal and vascular dysfunction in the retina, and later by neovascularization that leads to further deterioration of functional vision. Despite the availability of current treatments, diabetic retinopathy remains the leading cause of vision loss in working-age adults, those between the ages of 20 and 74. Existing treatment with anti-VEGF agents, although shown to be effective, are limited by short therapeutic half-lives, which then require frequent intravitreal injections over the patient's lifetime, resulting in increased risk of associated adverse events and significant treatment burden. Due to the burden of treatment, patients often do not closely adhere to treatment regimens and experience sub-optimal outcomes and a decline in vision.

Official Title

A Phase 2, Randomized, Controlled, Dose-escalation Study to Evaluate the Efficacy, Safety, and Tolerability of RGX-314 Gene Therapy Delivered Via a Single Suprachoroidal Space (SCS) Injections in Participants With Diabetic Retinopathy (DR) With and Without Center Involved-Diabetic Macular Edema (CI-DME)(ALTITUDE)

Quick Facts

Study Start:2020-11-20
Study Completion:2026-09
Study Type:Not specified
Phase:Not Applicable
Enrollment:Not specified
Status:ACTIVE_NOT_RECRUITING

Study ID

NCT04567550

Participation Criteria

Researchers look for people who fit a certain description, called eligibility criteria. Some examples of these criteria are a person's general health condition or prior treatments.

Ages Eligible for Study:25 Years to 89 Years
Sexes Eligible for Study:ALL
Accepts Healthy Volunteers:No
Standard Ages:ADULT, OLDER_ADULT
Inclusion CriteriaExclusion Criteria
  1. * Patients 25-89 years of age with a diabetic retinopathy (DR) diagnosis of nonproliferative diabetic retinopathy (NPDR) and proliferative diabetic retinopathy (PDR) secondary to diabetes mellitus Type 1 or 2 for which PRP or anti-VEGF injections can be safely deferred for at least 6 months
  2. * HbA1c \< 12%.
  3. * Best corrected visual acuity (BCVA) Early Treatment Diabetic Retinopathy Study (ETDRS) letter score in the study eye of ≥69 letters (approximate Snellen equivalent of 20/40 or better).
  4. * Prior history of CI-DME in the study eye is acceptable.
  5. * Must be willing and able to provide written, signed informed consent.
  1. * Neovascularization in the study eye from a cause other than DR.
  2. * Presence of any active CI-DME.
  3. * Active or history of retinal detachment in the study eye.
  4. * Any evidence or documented history of PRP or retinal laser in the study eye.
  5. * Patients who had a prior vitrectomy surgery.
  6. * Women of childbearing potential.

Contacts and Locations

Study Locations (Sites)

Retinal Research Institute, LLC
Phoenix, Arizona, 85014
United States
Barnet Dulaney Perkins Eye Center
Phoenix, Arizona, 85016
United States
California Retina Consultants
Bakersfield, California, 93309
United States
Retina-Vitreous Associates Medical Group
Beverly Hills, California, 90017
United States
Retinal Diagnostic Center
Campbell, California, 95008
United States
Northern California Retina Vitreous Associates Medical Group, Inc.
Mountain View, California, 94040
United States
California Eye Specialists Medical Group, Inc
Pasadena, California, 91107
United States
Retinal Consultants San Diego
Poway, California, 92064
United States
California Retina Consultants
Santa Barbara, California, 93103
United States
Southeast Retina Center, PC
Augusta, Georgia, 30909
United States
University Retina and Macula Associates, PC
Oak Forest, Illinois, 60452
United States
Springfield Clinic
Springfield, Illinois, 62702
United States
Wilmer Eye Institute/Johns Hopkins University School of Medicine
Baltimore, Maryland, 21287
United States
Cumberland Valley Retina Consultants
Hagerstown, Maryland, 21740
United States
Ophthalmic Consultants of Boston
Boston, Massachusetts, 02114
United States
Sierra Eye Associates
Reno, Nevada, 89502
United States
NJ Retina
Teaneck, New Jersey, 07666
United States
Vision Research Center Eye Associates of New Mexico
Albuquerque, New Mexico, 87109
United States
Duke University Eye Center
Durham, North Carolina, 27705
United States
Mid Atlantic Retina
Philadelphia, Pennsylvania, 19107
United States
Charles Retina Institute, P.C.
Germantown, Tennessee, 38138
United States
Retina Research Institute of Texas, LLC
Abilene, Texas, 79606
United States
Austin Clinical Research, LLC
Austin, Texas, 78750
United States
Star Retina
Burleson, Texas, 76028
United States
Retinal Consultants of Texas
The Woodlands, Texas, 77384
United States

Collaborators and Investigators

Sponsor: AbbVie

Study Record Dates

These dates track the progress of study record and summary results submissions to ClinicalTrials.gov. Study records and reported results are reviewed by the National Library of Medicine (NLM) to make sure they meet specific quality control standards before being posted on the public website.

Study Registration Dates

Study Start Date2020-11-20
Study Completion Date2026-09

Study Record Updates

Study Start Date2020-11-20
Study Completion Date2026-09

Terms related to this study

Keywords Provided by Researchers

  • DR
  • CI-DME

Additional Relevant MeSH Terms

  • Diabetic Retinopathy (DR)
  • Center-Involved Diabetic Macular Edema (CI-DME)