RECRUITING

A Study to Evaluate Tovorafenib in Pediatric and Young Adult Participants With Relapsed or Progressive Low-Grade Glioma and Advance Solid Tumors

Description

This is a Phase 2, multi center, open-label study to evaluate the safety and efficacy of Type II RAF (tovorafenib) in pediatric participants with low-grade glioma or advanced solid tumors. Qualifying genomic alterations will be identified through molecular assays as routinely performed at Clinical Laboratory Improvement Amendments (CLIA) of 1988 or other similarly certified laboratories prior to enrollment into any of the arms. The study will consist of a screening period, a treatment period, a long-term extension phase, end of treatment (EOT) visit(s), a safety follow-up visit, and long-term follow-up assessments.

Study Overview

Study Details

Study overview

This is a Phase 2, multi center, open-label study to evaluate the safety and efficacy of Type II RAF (tovorafenib) in pediatric participants with low-grade glioma or advanced solid tumors. Qualifying genomic alterations will be identified through molecular assays as routinely performed at Clinical Laboratory Improvement Amendments (CLIA) of 1988 or other similarly certified laboratories prior to enrollment into any of the arms. The study will consist of a screening period, a treatment period, a long-term extension phase, end of treatment (EOT) visit(s), a safety follow-up visit, and long-term follow-up assessments.

FIREFLY-1: A Phase 2, Open-Label, Multicenter Study to Evaluate the Safety and Efficacy of the Oral Pan-RAF Inhibitor DAY101 in Pediatric Patients With RAF-Altered, Recurrent or Progressive Low-Grade Glioma and Advanced Solid Tumors

A Study to Evaluate Tovorafenib in Pediatric and Young Adult Participants With Relapsed or Progressive Low-Grade Glioma and Advance Solid Tumors

Condition
Low-grade Glioma
Intervention / Treatment

-

Contacts and Locations

San Francisco

UCSF Benioff Children's Hospital, San Francisco, California, United States, 94143

Washington

Children's National Medical Center, Washington, District of Columbia, United States, 20010

Chicago

Lurie Children's Hospital of Chicago, Chicago, Illinois, United States, 60611

Baltimore

Johns Hopkins Hospital, Baltimore, Maryland, United States, 21231

Boston

Dana-Farber Cancer Institute, Boston, Massachusetts, United States, 02215

Ann Arbor

CS Mott Children's Hospital, Ann Arbor, Michigan, United States, 48109

Saint Louis

St. Louis Children's Hospital, Saint Louis, Missouri, United States, 63110

New York

NYU Langone Health, New York, New York, United States, 10016

Durham

Duke Cancer Center, Durham, North Carolina, United States, 27710

Portland

Doernbecher Children's Hospital Oregon & Health Science University, Portland, Oregon, United States, 97239

Participation Criteria

Researchers look for people who fit a certain description, called eligibility criteria. Some examples of these criteria are a person's general health condition or prior treatments.

For general information about clinical research, read Learn About Studies.

Eligibility Criteria

  • * Low Grade Glioma \& Low-Grade Glioma Extension: a relapsed or progressive LGG with documented known activating BRAF alteration.
  • * Advanced Solid Tumor: locally advanced or metastatic solid tumor with documented known or expected to be activating RAF fusion.
  • * Participants must have histopathologic verification of malignancy at either original diagnosis or relapse.
  • * Must have received at least one line of prior systemic therapy and have documented evidence of radiographic progression.
  • * Must have at least 1 measurable lesion as defined by RANO (Arms 1 \& 2) or RECIST v1.1 (Arm 3) criteria
  • * Participant's tumor has additional previously-known activating molecular alterations.
  • * Participant has symptoms of without radiographically recurrent or radiographically progressive disease.
  • * Known or suspected diagnosis of neurofibromatosis type 1 (NF-1) via genetic testing or current diagnostic criteria.

Ages Eligible for Study

6 Months to 25 Years

Sexes Eligible for Study

ALL

Accepts Healthy Volunteers

No

Collaborators and Investigators

Day One Biopharmaceuticals, Inc.,

Study Record Dates

2027-05-31