RECRUITING

4D-710 in Adult Patients with Cystic Fibrosis

Description

This is a Phase 1/2 multicenter, open-label, single dose trial of 4D-710 investigational gene therapy in adults with cystic fibrosis.

Study Overview

Study Details

Study overview

This is a Phase 1/2 multicenter, open-label, single dose trial of 4D-710 investigational gene therapy in adults with cystic fibrosis.

An Open-label, Phase 1/2 Trial of Gene Therapy 4D-710 in Adults with Cystic Fibrosis

4D-710 in Adult Patients with Cystic Fibrosis

Condition
Cystic Fibrosis Lung
Intervention / Treatment

-

Contacts and Locations

Birmingham

University of Alabama Child Health Research Unit, Birmingham, Alabama, United States, 35233

San Francisco

University of California San Francisco, San Francisco, California, United States, 94143

Denver

National Jewish Health, Denver, Colorado, United States, 80206

Gainesville

University of Florida, Gainesville, Florida, United States, 32610

Chicago

Northwestern Memorial Hospital, Chicago, Illinois, United States, 60611

Kansas City

University of Kansas Medical Center, Kansas City, Kansas, United States, 66160

Boston

Massachusetts General Hospital, Boston, Massachusetts, United States, 02114

Boston

Boston Children's Hospital, Boston, Massachusetts, United States, 02115

Chapel Hill

University of North Carolina at Chapel Hill, Chapel Hill, North Carolina, United States, 27599

Cleveland

Rainbow Babies and Children's Hospital/University Hospitals Cleveland Medical Center, Cleveland, Ohio, United States, 44146

Participation Criteria

Researchers look for people who fit a certain description, called eligibility criteria. Some examples of these criteria are a person's general health condition or prior treatments.

For general information about clinical research, read Learn About Studies.

Eligibility Criteria

    Ages Eligible for Study

    18 Years to

    Sexes Eligible for Study

    ALL

    Accepts Healthy Volunteers

    No

    Collaborators and Investigators

    4D Molecular Therapeutics,

    Alan H. Cohen, MD, STUDY_DIRECTOR, 4D Molecular Therapeutics

    Study Record Dates

    2030-01