RECRUITING

24 Weeks Double-blind Randomized Placebo-controlled Trial to Evaluate Efficacy, PK, Safety of LOU064 in Adolescents (12 - <18) With CSU and Inadequate Response to H1-antihistamine Followed by Optional 3 Years Open-label Extension and an Optional 3 Years Safety Long-term Treatment-free Follow-up

Study Overview

This clinical trial focuses on testing the efficacy of different digital interventions to promote re-engagement in cancer-related long-term follow-up care for adolescent and young adult (AYA) survivors of childhood cancer.

Description

The purpose of this trial is: 1. to assess the efficacy, pharmacokinetics, and safety of remibrutinib vs. placebo in adolescents from 12 to \< 18 years of age suffering from chronic spontaneous urticaria inadequately controlled by H1-antihistamines 2. to collect long-term efficacy, safety and tolerability data on remibrutinib in adolescents after having completed 24 weeks of treatment 3. to collect safety data in this population for up to three years after the last dose of study treatment

Official Title

A Double-blind, Randomized, Placebo-controlled Trial to Evaluate the Efficacy, Pharmacokinetics and Safety of Remibrutinib (LOU064) for 24 Weeks in Adolescents From 12 to Less Than 18 Years of Age With Chronic Spontaneous Urticaria Inadequately Controlled by H1-antihistamines Followed by an Optional Open-label Extension for up to Another 3 Years and an Optional Safety Long-term Treatment-free Follow-up Period for up to an Additional 3 Years

Quick Facts

Study Start:2023-07-11
Study Completion:2032-02-04
Study Type:Not specified
Phase:Not Applicable
Enrollment:Not specified
Status:RECRUITING

Study ID

NCT05677451

Participation Criteria

Researchers look for people who fit a certain description, called eligibility criteria. Some examples of these criteria are a person's general health condition or prior treatments.

Ages Eligible for Study:12 Years to 17 Years
Sexes Eligible for Study:ALL
Accepts Healthy Volunteers:No
Standard Ages:CHILD
Inclusion CriteriaExclusion Criteria
  1. * Male and female adolescent participants aged \>= 12 to \< 18 years of age at the time of signing the informed consent
  2. * CSU duration for \>= 6 months prior to screening (defined as the onset of CSU determined by the investigator based on all available supporting documentation)
  3. * Diagnosis of CSU inadequately controlled by second-generation H1-AH at the time of randomization defined as:
  4. * The presence of itch and hives for ≥ 6 consecutive weeks prior to screening despite the use of second-generation H1-AH during this time period according to local treatment guidelines
  5. * UAS7 score (range 0 - 42) \>= 16, ISS7 score (range 0 - 21) \>= 6 and HSS7 score (range 0 - 21) \>= 6 during the 7 days prior to randomization (Day 1)
  6. * Documentation of hives within three months before randomization (either at screening and/or at randomization; or documented in the participants' medical history)
  1. * Previous use of remibrutinib or other BTK inhibitors
  2. * Significant bleeding risk or coagulation disorders
  3. * History of gastrointestinal bleeding
  4. * Requirement for anti-platelet medication, except for acetylsalicylic acid up to 100 mg/d or clopidogrel up to 75 mg/d. The use of dual anti-platelet therapy (e.g., acetylsalicylic acid + clopidogrel) is prohibited
  5. * History or current hepatic disease
  6. * Evidence of clinically significant cardiovascular, neurological, psychiatric, pulmonary, renal, hepatic, endocrine, metabolic, hematological disorders, gastrointestinal disease or immunodeficiency that, in the investigator's opinion, would compromise the safety of the participant, interfere with the interpretation of the study results or otherwise preclude participation or protocol adherence of the participant
  7. * History of hypersensitivity to any of the study drugs or its excipients or to drugs of similar chemical classes
  8. * Participants having a clearly defined predominant or sole trigger of their chronic urticaria (chronic inducible urticaria) including urticaria factitia (symptomatic dermographism), cold-, heat-, solar-, pressure-, delayed pressure-, aquagenic-, cholinergic-, or contact-urticaria
  9. * Other diseases with symptoms of urticaria or angioedema, including but not limited to urticaria vasculitis, urticaria pigmentosa, erythema multiforme, mastocytosis, hereditary angioedema, or drug-induced urticaria
  10. * Any other skin disease associated with chronic itching that might influence in the investigator's opinion the study evaluations and results, e.g., atopic dermatitis, bullous pemphigoid, dermatitis herpetiformis, senile pruritus or psoriasis

Contacts and Locations

Study Contact

Novartis Pharmaceuticals
CONTACT
1-888-669-6682
novartis.email@novartis.com
Novartis Pharmaceuticals
CONTACT
+41613241111

Principal Investigator

Novartis Pharmaceuticals
STUDY_DIRECTOR
Novartis Pharmaceuticals

Study Locations (Sites)

Kern Research
Bakersfield, California, 93301
United States
Pediatric Dermatology of Miami at the Pediatric CoE
Coral Gables, Florida, 33134
United States
Treasure Valley Medical Research
Boise, Idaho, 83706
United States
Northshore University Health System
Glenview, Illinois, 60077
United States
Allergy and Asthma Specialist P S C
Owensboro, Kentucky, 42301
United States
Toledo Institute of Clinical Research
Toledo, Ohio, 43617
United States
Allergy Asthma and Clinical Research
Oklahoma City, Oklahoma, 73120
United States
Allergy and Clinical Immunology Associates
Pittsburgh, Pennsylvania, 15241
United States
RFSA Dermatology
San Antonio, Texas, 78213
United States
Allergy Associates of Utah
Sandy, Utah, 84093
United States
Seattle Allergy and Asthma Rsch
Seattle, Washington, 98115
United States

Collaborators and Investigators

Sponsor: Novartis Pharmaceuticals

  • Novartis Pharmaceuticals, STUDY_DIRECTOR, Novartis Pharmaceuticals

Study Record Dates

These dates track the progress of study record and summary results submissions to ClinicalTrials.gov. Study records and reported results are reviewed by the National Library of Medicine (NLM) to make sure they meet specific quality control standards before being posted on the public website.

Study Registration Dates

Study Start Date2023-07-11
Study Completion Date2032-02-04

Study Record Updates

Study Start Date2023-07-11
Study Completion Date2032-02-04

Terms related to this study

Keywords Provided by Researchers

  • BTK inhibitor
  • Chronic spontaneous urticaria
  • Urticaria activity score
  • Hives severity score
  • Itch severity score

Additional Relevant MeSH Terms

  • Chronic Spontaneous Urticaria