RECRUITING

A Study of SIPLIZUMAB in AILD and LT Patients

Study Overview

This clinical trial focuses on testing the efficacy of different digital interventions to promote re-engagement in cancer-related long-term follow-up care for adolescent and young adult (AYA) survivors of childhood cancer.

Description

There is a significant unmet need for safe and effective therapeutic approaches to prevent immune-mediated graft injury and its complications in liver transplant (LT) recipients with autoimmune liver disease (AILD) including autoimmune hepatitis and primary sclerosing cholangitis. Siplizumab is an anti-cluster of differentiation 2 (CD2) monoclonal antibody that has demonstrated a favorable safety profile of siplizumab in over 779 human subjects and has been shown to target memory T cells-a key driver in the immune processes surrounding rejection and autoimmunity post LT in AILD. The purpose of this pilot, open-label phase 1 study is to determine the safety of siplizumab for induction in patients with AILD undergoing LT. Up to eight (8) subjects will receive siplizumab 0.6 mg/kg/dose on the day of transplant (Day 0) and Day 4 post-transplant, for a total of two doses. All subjects will be followed in the study for 12 months post-LT.

Official Title

A 12-Month, Open-Label Study Evaluating Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of Siplizumab As Induction Therapy in Patients with Autoimmune Liver Diseases Undergoing Liver Transplantation (SET-SAIL)

Quick Facts

Study Start:2024-09-11
Study Completion:2026-03-31
Study Type:Not specified
Phase:Not Applicable
Enrollment:Not specified
Status:RECRUITING

Study ID

NCT06455280

Participation Criteria

Researchers look for people who fit a certain description, called eligibility criteria. Some examples of these criteria are a person's general health condition or prior treatments.

Ages Eligible for Study:18 Years
Sexes Eligible for Study:ALL
Accepts Healthy Volunteers:No
Standard Ages:ADULT, OLDER_ADULT
Inclusion CriteriaExclusion Criteria
  1. 1. Able to provide informed consent
  2. 2. Age ≥ 18 years old
  3. 3. Clinical diagnosis of AIH and/or PSC
  4. 4. Listed for liver transplantation
  5. 5. Epstein-Barr virus (EBV) seropositive within 12 months of screening
  1. 1. Presence or history of significant liver disease other than AIH or PSC, including viral hepatitis, alcohol-related liver disease and biopsy-proven non-alcoholic steatohepatitis
  2. 2. Prior transplant
  3. 3. Listed for multiorgan transplant
  4. 4. Acute liver failure
  5. 5. Known malignancy, including cholangiocarcinoma and hepatocellular carcinoma
  6. 6. Other investigational products in the last 30 days or 5 half lives
  7. 7. Pregnant/lactating or unwilling to use contraception
  8. 8. Leukopenia (WBC less than 2,000/mm3
  9. 9. Absolute lymphocyte count \< 200/mm3
  10. 10. Sero-positive for HIV-1
  11. 11. Hepatitis C Virus (HCV) antibody or RNA positive (within 6 months of screening)
  12. 12. HBsAg, hepatitis B virus (HBV) DNA or HBcAb positive (within 6 months of screening)
  13. 13. Alcohol use exceeding 30g/day for men or 20g/day for women, and/or known phosphatidylethanol (PETH) level \>80 in the 3 months prior to LT
  14. 14. Untreated latent TB infection as detected by QuantiFERON Gold Plus Interferon Gamma Release Assay (IGRA) (or current standard interferon gamma release assay for TB)
  15. 15. Receipt of any live-attenuated vaccine within 2 months of transplant.
  16. 1. Renal failure with dialysis or with estimated glomerular filtration rate (eGFR) \< 30 at the time of LT
  17. 2. Model for end-stage liver disease (MELD)-Na score \>30
  18. 3. Donor features of Donation after Cardiac Death (DCD), HCV Ab or nucleic acid testing (NAT+), HBcAb or HBsAg+, or blood types A, B, and O incompatible organ

Contacts and Locations

Study Contact

Theresa Lukose, PharmD
CONTACT
212-305-3839
tt2103@cumc.columbia.edu
Amanda Alonso, MHA
CONTACT
212-342-0261
aa2974@cumc.columbia.edu

Principal Investigator

Elizabeth Verna, MD
PRINCIPAL_INVESTIGATOR
Columbia University Irving Medical Center/ New York Presbyterian Hospital

Study Locations (Sites)

Columbia University Irving Medical Center/NewYork-Presbyterian Hospital
New York, New York, 10032
United States

Collaborators and Investigators

Sponsor: Elizabeth C. Verna

  • Elizabeth Verna, MD, PRINCIPAL_INVESTIGATOR, Columbia University Irving Medical Center/ New York Presbyterian Hospital

Study Record Dates

These dates track the progress of study record and summary results submissions to ClinicalTrials.gov. Study records and reported results are reviewed by the National Library of Medicine (NLM) to make sure they meet specific quality control standards before being posted on the public website.

Study Registration Dates

Study Start Date2024-09-11
Study Completion Date2026-03-31

Study Record Updates

Study Start Date2024-09-11
Study Completion Date2026-03-31

Terms related to this study

Keywords Provided by Researchers

  • Autoimmune Liver Disease
  • Liver Transplant Disorder
  • Autoimmune Hepatitis
  • Primary Sclerosing Cholangitis
  • End Stage Liver DIsease
  • Cirrhosis, Liver

Additional Relevant MeSH Terms

  • Autoimmune Liver Disease
  • Liver Transplant Disorder
  • Autoimmune Hepatitis
  • Primary Sclerosing Cholangitis
  • End Stage Liver DIsease
  • Cirrhosis, Liver