RECRUITING

Study of Ravulizumab in Pediatric Participants With Primary IgAN

Description

The primary objective of this study is to characterize the pharmacokinetics (PK) and pharmacodynamics (PD) of treatment with ravulizumab IV in pediatric participants to support the extrapolation of efficacy from the adult population.

Study Overview

Study Details

Study overview

The primary objective of this study is to characterize the pharmacokinetics (PK) and pharmacodynamics (PD) of treatment with ravulizumab IV in pediatric participants to support the extrapolation of efficacy from the adult population.

A Phase 3, Open-Label, Multicenter Study to Evaluate the Pharmacokinetics, Pharmacodynamics, Efficacy, and Safety of Ravulizumab in Pediatric Participants (2 to < 18 Years of Age) With Primary Immunoglobulin A Nephropathy (IgAN)

Study of Ravulizumab in Pediatric Participants With Primary IgAN

Condition
IgAN
Intervention / Treatment

-

Contacts and Locations

Aurora

Research Site, Aurora, Colorado, United States, 80045

Participation Criteria

Researchers look for people who fit a certain description, called eligibility criteria. Some examples of these criteria are a person's general health condition or prior treatments.

For general information about clinical research, read Learn About Studies.

Eligibility Criteria

  • * Participant must be 2 to \< 18 years of age at the time of signing the informed consent or assent.
  • * Stable and maximum allowed or tolerated RASI (ACEI and/or ARB) dose for ≥ 3 months prior to Screening with no planned change during Screening through Week 106.
  • * UPCR ≥ 0.5 g/g from the mean of 3 first morning voids (FMV) collected within 1 week during the Screening Period
  • * Estimated GFR ≥ 30 mL/min/1.73 m2 during Screening
  • * Meningococcal infection vaccine
  • * Haemophilus influenzae type b and Streptococcus pneumoniae vaccine
  • * Diagnosis of rapidly progressive glomerulonephritis
  • * Secondary forms of IgAN not in the context of primary IgAN or IgAV
  • * Concomitant clinically significant renal disease other than IgAN or IgAVN
  • * Uncontrolled diabetes mellitus with HbA1c \> 8.5%
  • * History of kidney transplant or planned kidney transplant during the Primary Evaluation Period.
  • * History of other solid organ (heart, lung, small bowel, pancreas, or liver) or bone marrow transplant
  • * Splenectomy or functional asplenia
  • * Participants with nephrotic syndrome receiving albumin infusions or with acute kidney injury requiring dialysis within the last 6 months prior to Screening.
  • * Hemolytic uremic syndrome diagnosed any time prior to Screening.
  • * Planned urological surgery expected to influence kidney function within the study time frame.
  • * Congenital immunodeficiency
  • * Active systemic bacterial, viral, or fungal infection within 14 days prior to enrollment
  • * Received biologics for the treatment of IgAN or IgAVN ≤ 6 months prior to Screening

Ages Eligible for Study

2 Years to 18 Years

Sexes Eligible for Study

ALL

Accepts Healthy Volunteers

No

Collaborators and Investigators

Alexion Pharmaceuticals, Inc.,

Study Record Dates

2029-03-08