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Showing 1-1 of 1 trials for Pids-linked-to-pi3k
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Long-term Safety and Efficacy of Leniolisib in PIDs With Immune Dysregulation

Maryland

This is an open-label extension (OLE) study to extend treatment to patients with primary immunodeficiency (PID) disorders linked to phosphoinositide 3-kinase delta signaling who participated in a prior study of leniolisib, LE 7201. The primary objective is to assess long-term safety and tolerability of leniolisib. Secondary and exploratory objectives include various efficacy and immunophenotyping measures for leniolisib.