Treatment Trials

3 Clinical Trials for Various Conditions

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      RECRUITING
      Myotonic Dystrophy Family Registry
      Description

      The Myotonic Dystrophy Family Registry (MDFR) is an online, patient-entered database that collects information on myotonic dystrophy (DM) to aid researchers in developing new, effective treatments and help identify participants for research studies and clinical trials.

      Conditions
      Myotonic DystrophyCongenital Myotonic DystrophyMyotonic Dystrophy 1Myotonic Dystrophy 2Dystrophia MyotonicaDystrophia Myotonica 1Dystrophia Myotonica 2Myotonia DystrophicaMyotonic Dystrophy, CongenitalMyotonic Myopathy, ProximalPROMM (Proximal Myotonic Myopathy)Proximal Myotonic MyopathySteinert DiseaseSteinert Myotonic DystrophySteinert's DiseaseMyotonia Atrophica
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      RECRUITING
      Safety and Efficacy of Tideglusib in Congenital or Childhood Onset Myotonic Dystrophy
      Description

      This is an open-label phase 2/3 study for individuals with Congenital Myotonic Dystrophy (Congenital DM1) who participated in the preceding AMO-02-MD-2-003 study or individuals with either Congenital or Childhood Onset DM1 who are treatment naïve.

      Conditions
      Congenital Myotonic Dystrophy
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      COMPLETED
      Efficacy and Safety of Tideglusib in Congenital Myotonic Dystrophy
      Description

      This is a randomized, multicenter, double-blind, placebo-controlled, Phase 2/3 study of patients (aged 6 to 16 years) diagnosed with Congenital Myotonic Dystrophy (Congenital DM1).

      Conditions
      Congenital Myotonic Dystrophy
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