The Mucopolysaccharidosis I (MPS I) Registry is an ongoing, observational database that tracks the outcomes of patients with MPS I. The data collected by the MPS I Registry will provide information to better characterize the natural history and progression of MPS I as well as the clinical responses of patients receiving enzyme replacement therapy, such as Aldurazyme (Recombinant Human Alpha-L-Iduronidase), or other treatment modalities. The objectives of the Registry are: * To evaluate the long-term effectiveness and safety of Aldurazyme® (laronidase) * To characterize and describe the MPS I population as a whole, including the variability, progression, and natural history of MPS I * To help the MPS I medical community with the development of recommendations for monitoring patients and reports on patient outcomes to optimize patient care
Mucopolysaccharidosis I (MPS I)
The Mucopolysaccharidosis I (MPS I) Registry is an ongoing, observational database that tracks the outcomes of patients with MPS I. The data collected by the MPS I Registry will provide information to better characterize the natural history and progression of MPS I as well as the clinical responses of patients receiving enzyme replacement therapy, such as Aldurazyme (Recombinant Human Alpha-L-Iduronidase), or other treatment modalities. The objectives of the Registry are: * To evaluate the long-term effectiveness and safety of Aldurazyme® (laronidase) * To characterize and describe the MPS I population as a whole, including the variability, progression, and natural history of MPS I * To help the MPS I medical community with the development of recommendations for monitoring patients and reports on patient outcomes to optimize patient care
Mucopolysaccharidosis I (MPS I) Registry
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Phoenix Children's Hospital- Site Number : 840003, Phoenix, Arizona, United States, 85013
Arkansas Childrens Hospital- Site Number : 840109, Little Rock, Arkansas, United States, 72202
Southern California Permanente Medical Group- Site Number : 840108, Los Angeles, California, United States, 90027
USC Health Sciences Center Dept of Genetics- Site Number : 840082, Los Angeles, California, United States, 90033
Children's Hospital Oakland- Site Number : 840029, Oakland, California, United States, 94609
Children's Hospital of Orange County- Site Number : 840074, Orange, California, United States, 92868
Stanford Unviersity MC Dept of Genetics- Site Number : 840022, Palo Alto, California, United States, 94305
UC Davis MIND Institute- Site Number : 840010, Sacramento, California, United States, 95817
Loma Linda University Children's Hospital- Site Number : 840117, San Bernardino, California, United States, 92408
University of California at San Diego- Site Number : 840007, San Diego, California, United States, 92093
Researchers look for people who fit a certain description, called eligibility criteria. Some examples of these criteria are a person's general health condition or prior treatments.
For general information about clinical research, read Learn About Studies.
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Genzyme, a Sanofi Company,
Medical Monitor, STUDY_DIRECTOR, Genzyme, a Sanofi Company
2034-01-31