RECRUITING

NBIAready: Online Collection of Natural History Patient-reported Outcome Measures

Study Overview

This clinical trial focuses on testing the efficacy of different digital interventions to promote re-engagement in cancer-related long-term follow-up care for adolescent and young adult (AYA) survivors of childhood cancer.

Description

The purpose of this study is to learn more about Neurodegeneration with Brain Iron Accumulation (NBIA) Disorders. Data is being collected on three types of NBIA disorders: Pantothenate Kinase-Associated Neurodegeneration (PKAN), PLA2G6-associated Neurodegeneration (PLAN) and Beta-propeller Protein-associated Neurodegeneration (BPAN). The study will (1) collect information about how symptoms and findings in NBIA change over time and (2) identify measures of NBIA that can be used in future clinical trials. Participants will follow links to a secure website every 6 months for a period of 5-10 years to electronically complete a set of rating scales as related to their NBIA disorder.

Official Title

NBIAready: Online Collection of Natural History Patient-reported Outcome Measures

Quick Facts

Study Start:2015-04
Study Completion:2025-04
Study Type:Not specified
Phase:Not Applicable
Enrollment:Not specified
Status:RECRUITING

Study ID

NCT02587858

Participation Criteria

Researchers look for people who fit a certain description, called eligibility criteria. Some examples of these criteria are a person's general health condition or prior treatments.

Ages Eligible for Study:Not specified
Sexes Eligible for Study:ALL
Accepts Healthy Volunteers:No
Standard Ages:CHILD, ADULT, OLDER_ADULT
Inclusion CriteriaExclusion Criteria
  1. * Diagnosis of PKAN, PLAN or BPAN confirmed by gene testing and/or clinical features.
  2. * Ability to access a computer with internet services or a phone approximately once every 6 months for up to 10 years to enter data.
  1. * Individuals who are not fluent in reading and communicating in English.

Contacts and Locations

Study Contact

Alison C Freed, BA
CONTACT
503 494 6838
freeal@ohsu.edu
Allison M Gregory, MS, CGC
CONTACT
503 494 4344
gregorya@ohsu.edu

Principal Investigator

Susan J Hayflick, MD
PRINCIPAL_INVESTIGATOR
Oregon Health and Science University

Study Locations (Sites)

Oregon Health & Science University
Portland, Oregon, 97239-3098
United States

Collaborators and Investigators

Sponsor: Susan J. Hayflick

  • Susan J Hayflick, MD, PRINCIPAL_INVESTIGATOR, Oregon Health and Science University

Study Record Dates

These dates track the progress of study record and summary results submissions to ClinicalTrials.gov. Study records and reported results are reviewed by the National Library of Medicine (NLM) to make sure they meet specific quality control standards before being posted on the public website.

Study Registration Dates

Study Start Date2015-04
Study Completion Date2025-04

Study Record Updates

Study Start Date2015-04
Study Completion Date2025-04

Terms related to this study

Keywords Provided by Researchers

  • NBIA
  • PKAN
  • brain iron
  • Neurodegeneration with Brain Iron Accumulation
  • Hallervorden Spatz Syndrome
  • Pantothenate Kinase Associated Neurodegeneration
  • PLAN
  • INAD
  • PLA2G6-associated neurodegeneration
  • BPAN
  • Beta-propeller Protein-associated neurodegenration
  • WDR45
  • PLA2G6

Additional Relevant MeSH Terms

  • Neurodegeneration With Brain Iron Accumulation (NBIA)