RECRUITING

RGX-314 Gene Therapy Administered in the Suprachoroidal Space for Participants With Neovascular Age-Related Macular Degeneration (nAMD)

Study Overview

This clinical trial focuses on testing the efficacy of different digital interventions to promote re-engagement in cancer-related long-term follow-up care for adolescent and young adult (AYA) survivors of childhood cancer.

Description

This interventional study is being conducted with an investigational gene therapy treatment called ABBV-RGX-314 (also known as RGX-314) and is being developed as a potential one-time gene therapy treatment for neovascular (wet) age-related macular degeneration (wet AMD or nAMD). The typical treatment for nAMD is frequent injections of anti-VEGF therapy. Researchers are testing ABBV-RGX-314 to see if it has similar effects as the current approved standard of care, such as Lucentis® or Eylea® injections. The duration of this study will be up to 52 weeks or for ranibizumab control participants who cross over to ABBV-RGX-314 after week 52, up to 80 weeks post-randomization. The primary outcome measure for this investigational study is to evaluate the mean change in best-corrected visual acuity (BCVA) for ABBV-RGX-314 compared with ranibizumab monthly at the Week 40 visit.

Official Title

A Phase 2, Randomized, Dose-escalation, Ranibizumab-controlled Study to Evaluate the Efficacy, Safety, and Tolerability of RGX-314 Gene Therapy Delivered Via One or Two Suprachoroidal Space (SCS) Injections in Participants With Neovascular Age-Related Macular Degeneration (nAMD) (AAVIATE)

Quick Facts

Study Start:2020-08-25
Study Completion:2027-02
Study Type:Not specified
Phase:Not Applicable
Enrollment:Not specified
Status:RECRUITING

Study ID

NCT04514653

Participation Criteria

Researchers look for people who fit a certain description, called eligibility criteria. Some examples of these criteria are a person's general health condition or prior treatments.

Ages Eligible for Study:50 Years to 89 Years
Sexes Eligible for Study:ALL
Accepts Healthy Volunteers:No
Standard Ages:ADULT, OLDER_ADULT
Inclusion CriteriaExclusion Criteria
  1. * Age \>/= 50 and \</= 89
  2. * Diagnosis of CNV secondary to age-related macular degeneration in the study eye.
  3. * Participants must have demonstrated a meaningful response to anti-VEGF therapy.
  4. * Willing and able to provide written, signed informed consent for this study.
  1. * CNV or macular edema in the study eye secondary to any causes other than AMD.
  2. * Subfoveal fibrosis or atrophy in study eye.
  3. * Participants who have had a prior vitrectomy.
  4. * Active or history of retinal detachment in the study eye.
  5. * History of intravitreal therapy in the study eye, such as intravitreal steroid injection or investigational product (IP), other than anti-VEGF therapy, in the 6 months prior to study entry.
  6. * Received any gene therapy.
  7. * Any condition preventing visualization of the fundus or VA improvement in the study eye, eg, cataract.
  8. * History of intraocular surgery in the study eye within 12 weeks of study entry.
  9. * Receipt of any IP within 30 days of study entry or 5 half-lives of the IP.
  10. * Myocardial infarction, cerebrovascular accident, or transient ischemic attacks within 6 months of study entry.
  11. * Cohorts 1 - 5 only: Uncontrolled glaucoma in the study eye.
  12. * Active or history of glaucoma or ocular hypertension (steroid-induced ocular hypertension (Cohort 7 only)) in the study eye.
  13. * Certain OCT characteristics including: Large Pigment Epithelial Detachments (PED), clinically significant Epiretinal Membrane (ERM) in the study eye at Visit 1.

Contacts and Locations

Study Contact

Patient Advocacy
CONTACT
1-866-860-0117
patientadvocacy@regenxbio.com

Principal Investigator

ABBVIE INC.
STUDY_DIRECTOR
AbbVie

Study Locations (Sites)

Retinal Research Institute /ID# 255925
Phoenix, Arizona, 85053
United States
California Retina Consultants - Bakersfield /ID# 255910
Bakersfield, California, 93309-1677
United States
Retina Vitreous Assoc Med Grp /ID# 255921
Beverly Hills, California, 90211
United States
Retinal Diagnostic Center /ID# 272275
Campbell, California, 95008
United States
Northern California Retina Vitreous Associates Medical Group, Inc /ID# 255920
Mountain View, California, 94040-4101
United States
Retina Consultants of San Diego /ID# 255911
Poway, California, 92064-2530
United States
California Retina Consultants - Santa Barbara /ID# 255923
Santa Barbara, California, 93103
United States
Southeast Retina Center /ID# 255912
Augusta, Georgia, 30909
United States
Springfield Clinic - First /ID# 272274
Springfield, Illinois, 62702
United States
Johns Hopkins Hospital /ID# 255919
Baltimore, Maryland, 21287
United States
Ophthalmic Consultants of Boston /ID# 255917
Boston, Massachusetts, 02114
United States
Sierra Eye Associates /ID# 255908
Reno, Nevada, 89502
United States
Eye Associates of New Mexico /ID# 255915
Albuquerque, New Mexico, 87109
United States
Duke University Medical Center /ID# 267646
Durham, North Carolina, 27710
United States
Mid Atlantic Retina /ID# 255906
Philadelphia, Pennsylvania, 19107
United States
Charles Retina Institute /ID# 255922
Germantown, Tennessee, 38138
United States
Tennessee Retina - Nashville /ID# 255918
Nashville, Tennessee, 37203-1513
United States
Retina Consultants - The Woodlands /ID# 255924
The Woodlands, Texas, 77384
United States

Collaborators and Investigators

Sponsor: AbbVie

  • ABBVIE INC., STUDY_DIRECTOR, AbbVie

Study Record Dates

These dates track the progress of study record and summary results submissions to ClinicalTrials.gov. Study records and reported results are reviewed by the National Library of Medicine (NLM) to make sure they meet specific quality control standards before being posted on the public website.

Study Registration Dates

Study Start Date2020-08-25
Study Completion Date2027-02

Study Record Updates

Study Start Date2020-08-25
Study Completion Date2027-02

Terms related to this study

Keywords Provided by Researchers

  • AMD
  • wet AMD
  • wAMD
  • nAMD

Additional Relevant MeSH Terms

  • Neovascular Age-Related Macular Degeneration (nAMD)