Study of Sparsentan Treatment in Pediatrics With Proteinuric Glomerular Diseases

Description

To evaluate the safety, efficacy and tolerability of sparsentan oral suspension and tablets, and assess changes in proteinuria after once-daily dosing over 108 weeks.

Conditions

Focal Segmental Glomerulosclerosis, Minimal Change Disease, Immunoglobulin A Nephropathy, IgA Vasculitis, Alport Syndrome

Study Overview

Study Details

Study overview

To evaluate the safety, efficacy and tolerability of sparsentan oral suspension and tablets, and assess changes in proteinuria after once-daily dosing over 108 weeks.

A Phase 2, Open-Label, Single-Arm, Cohort Study to Evaluate the Safety, Efficacy, and Pharmacokinetics of Sparsentan Treatment in Pediatric Subjects With Selected Proteinuric Glomerular Diseases

Study of Sparsentan Treatment in Pediatrics With Proteinuric Glomerular Diseases

Condition
Focal Segmental Glomerulosclerosis
Intervention / Treatment

-

Contacts and Locations

Los Angeles

Travere Investigational Site, Los Angeles, California, United States, 90048

Wilmington

Travere Investigational Site, Wilmington, Delaware, United States, 19803

Miami

Travere Investigational Site, Miami, Florida, United States, 33136

Miami

Travere Investigational Site, Miami, Florida, United States, 33155

Iowa City

Travere Investigational Site, Iowa City, Iowa, United States, 52242

Boston

Travere Investigational Site, Boston, Massachusetts, United States, 02111

Ann Arbor

Travere Investigational Site, Ann Arbor, Michigan, United States, 48109-5008

Minneapolis

Travere Investigational Site, Minneapolis, Minnesota, United States, 55454

Kansas City

Travere Investigational Site, Kansas City, Missouri, United States, 64108

Hackensack

Travere Investigational Site, Hackensack, New Jersey, United States, 07601

Participation Criteria

Researchers look for people who fit a certain description, called eligibility criteria. Some examples of these criteria are a person's general health condition or prior treatments.

For general information about clinical research, read Learn About Studies.

Eligibility Criteria

    Ages Eligible for Study

    1 Year to 17 Years

    Sexes Eligible for Study

    ALL

    Accepts Healthy Volunteers

    No

    Collaborators and Investigators

    Travere Therapeutics, Inc.,

    Radko Komers, MD, PhD, STUDY_DIRECTOR, Travere Therapeutics, Inc.

    Study Record Dates

    2025-06-01