Study to Evaluate the Safety and Efficacy of Daily Subcutaneous Metreleptin Treatment in Subjects With PL

Description

This is a Phase III, double-blind, placebo-controlled, safety and efficacy study of daily SC metreleptin in subjects with Partial Lipodystrophy.

Conditions

Partial Lipodystrophy

Study Overview

Study Details

Study overview

This is a Phase III, double-blind, placebo-controlled, safety and efficacy study of daily SC metreleptin in subjects with Partial Lipodystrophy.

A 12-Month Randomized, Multicenter, Double-Blind, Placebo-Controlled Phase 3 Study to Evaluate the Safety and Efficacy of Daily Subcutaneous Metreleptin Treatment in Subjects With Partial Lipodystrophy

Study to Evaluate the Safety and Efficacy of Daily Subcutaneous Metreleptin Treatment in Subjects With PL

Condition
Partial Lipodystrophy
Intervention / Treatment

-

Contacts and Locations

Birmingham

Amryt Research Site, University of Alabama, Birmingham, Alabama, United States, 35233

Boston

Massachusetts General Hospital, Boston, Massachusetts, United States, 02114

Ann Arbor

Amryt Research Site, University of Michigan, Ann Arbor, Michigan, United States, 48109

Rochester

Amryt Research Site, Mayo Clinic,, Rochester, Minnesota, United States, 55902

Columbia

Amryt Research Site, University of Missouri, Columbia, Missouri, United States, 65212

Columbus

Amryt Research Site, Endocrinology Research Associates Inc, Columbus, Ohio, United States, 43201

Columbus

Amryt Research Site, The Ohio State University Wexner Medical Center, Columbus, Ohio, United States, 43210

Philadelphia

Amryt Research Site, University of Pennsylvania, Philadelphia, Pennsylvania, United States, 19104

Dallas

Amryt Research Site, UT Southwestern Medical Center, Dallas, Texas, United States, 75390

Milwaukee

Amryt Research Site, Medical College of Wisconsin, Milwaukee, Wisconsin, United States, 53226

Participation Criteria

Researchers look for people who fit a certain description, called eligibility criteria. Some examples of these criteria are a person's general health condition or prior treatments.

For general information about clinical research, read Learn About Studies.

Eligibility Criteria

  • * Diagnosis of Familial Partial Lipodystrophy (FPLD)
  • * Previous treatment with metreleptin

Ages Eligible for Study

12 Years to

Sexes Eligible for Study

ALL

Accepts Healthy Volunteers

No

Collaborators and Investigators

Amryt Pharma,

Study Record Dates

2026-01-31