Cardiopulmonary Outcomes in Osteogenesis Imperfecta: BBD7708

Description

Osteogenesis imperfecta (OI) is a group of congenital and heritable bone disorders that currently affects at least 50,000 people in the United States. OI varies in severity from perinatally lethal to mild forms. The majority of cases is caused by a dominant mutation in type I collagen genes (COL1α1 and COL1α2), altering the quantity or quality of type I collagen. Although OI is typically characterized as a disease of the bone, it is perhaps more accurately described as a connective tissue disorder. Type I collagen is a major constituent of lung connective tissue. Respiratory insufficiency is the leading cause of death in patients with OI. Thus, it is important and necessary to understand the etiology of the restrictive pulmonary physiology in the OI population.

Conditions

Osteogenesis Imperfecta

Study Overview

Study Details

Study overview

Osteogenesis imperfecta (OI) is a group of congenital and heritable bone disorders that currently affects at least 50,000 people in the United States. OI varies in severity from perinatally lethal to mild forms. The majority of cases is caused by a dominant mutation in type I collagen genes (COL1α1 and COL1α2), altering the quantity or quality of type I collagen. Although OI is typically characterized as a disease of the bone, it is perhaps more accurately described as a connective tissue disorder. Type I collagen is a major constituent of lung connective tissue. Respiratory insufficiency is the leading cause of death in patients with OI. Thus, it is important and necessary to understand the etiology of the restrictive pulmonary physiology in the OI population.

Cardiopulmonary Outcomes in Osteogenesis Imperfecta: BBD7708

Cardiopulmonary Outcomes in Osteogenesis Imperfecta: BBD7708

Condition
Osteogenesis Imperfecta
Intervention / Treatment

-

Contacts and Locations

Los Angeles

University of California Los Angeles, Los Angeles, California, United States, 90095

Baltimore

Kennedy Krieger Institute / Hugo W. Moser Research Institute, Baltimore, Maryland, United States, 21205

New York

Hospital for Special Surgery, New York, New York, United States, 10021

Participation Criteria

Researchers look for people who fit a certain description, called eligibility criteria. Some examples of these criteria are a person's general health condition or prior treatments.

For general information about clinical research, read Learn About Studies.

Eligibility Criteria

  • * Individuals who are able to give informed consent or have a legally authorized representative capable of giving consent on the subject's behalf
  • * Individuals ages 18 and older of all races and sexes
  • * Individuals who have been diagnosed with OI clinically and/or genetically
  • * Individuals diagnosed with respiratory illness within 6 weeks of enrollment or undergoing diagnostic studies for an active illness.
  • * Individuals with other skeletal dysplasia or genetic diagnosis
  • * Individuals diagnosed with cardiopulmonary comorbidities that affect lung compliance

Ages Eligible for Study

18 Years to

Sexes Eligible for Study

ALL

Accepts Healthy Volunteers

No

Collaborators and Investigators

Baylor College of Medicine,

Vernon Sutton, MD, PRINCIPAL_INVESTIGATOR, Baylor College of Medicine

Kathleen Raggio, STUDY_CHAIR, Hospital for Special Surgery, New York

Study Record Dates

2026-09-01