BEACON: A Study Evaluating the Safety and Efficacy of BEAM-101 in Patients With Severe Sickle Cell Disease

Description

This is an open-label, single-arm, multicenter, Phase 1/2 study evaluating the safety and efficacy of the administration of autologous base edited CD34+ HSPCs (BEAM-101) in patients with severe SCD

Conditions

Sickle Cell Disease

Study Overview

Study Details

Study overview

This is an open-label, single-arm, multicenter, Phase 1/2 study evaluating the safety and efficacy of the administration of autologous base edited CD34+ HSPCs (BEAM-101) in patients with severe SCD

A Phase 1/2 Study Evaluating the Safety and Efficacy of a Single Dose of Autologous CD34+ Base Edited Hematopoietic Stem Cells (BEAM-101) in Patients With Sickle Cell Disease and Severe Vaso-Occlusive Crises (Beacon Trial)

BEACON: A Study Evaluating the Safety and Efficacy of BEAM-101 in Patients With Severe Sickle Cell Disease

Condition
Sickle Cell Disease
Intervention / Treatment

-

Contacts and Locations

Birmingham

University of Alabama at Birmingham, Birmingham, Alabama, United States, 35233

Palo Alto

Lucile Packard Children's Hospital at Standford, Palo Alto, California, United States, 94304

Jacksonville

Mayo Clinic Florida, Jacksonville, Florida, United States, 32224

Miami

University of Miami, Miami, Florida, United States, 33136-1005

Boston

Boston Children's Hospital, Boston, Massachusetts, United States, 02215

Detroit

Henry Ford Cancer Center, Detroit, Michigan, United States, 48202

Minneapolis

University of Minnesota, Minneapolis, Minnesota, United States, 55455

Saint Louis

Washington University School of Medicine in St. Louis, Saint Louis, Missouri, United States, 63110

New York

Columbia University Irving Medical Center, New York, New York, United States, 10032

Cleveland

University Hospitals Cleveland Medical Center, Cleveland, Ohio, United States, 44106

Participation Criteria

Researchers look for people who fit a certain description, called eligibility criteria. Some examples of these criteria are a person's general health condition or prior treatments.

For general information about clinical research, read Learn About Studies.

Eligibility Criteria

    Ages Eligible for Study

    18 Years to 35 Years

    Sexes Eligible for Study

    ALL

    Accepts Healthy Volunteers

    No

    Collaborators and Investigators

    Beam Therapeutics Inc.,

    Study Record Dates

    2027-02-01