RECRUITING

POEM-F for Achalasia International Study

Study Overview

This clinical trial focuses on testing the efficacy of different digital interventions to promote re-engagement in cancer-related long-term follow-up care for adolescent and young adult (AYA) survivors of childhood cancer.

Description

Per-oral endoscopic myotomy (POEM) has emerged as the endoscopic treatment of choice for achalasia, offering comparable symptom relief with laparoscopic Heller's cardiomyotomy. The main concern with POEM is the higher incidence of post-procedure gastroesophageal reflux disease (GERD), occurring in up to 50-60% of patients. In order to reduce the risk of GERD, endoscopic fundoplication has been developed as a novel procedure mimicking surgical anterior partial fundoplication that can be performed in the same session as POEM (POEM-F). Case series of POEM-F in patients with achalasia reported encouraging outcomes of low GERD rate of \~12% at 1 year. Prospective comparative data between POEM-F and conventional POEM on post-procedure GERD is current lacking. The investigators therefore designed an international multicenter prospective randomized study to investigate the efficacy of POEM-F. The investigators postulate that POEM-F could reduce the incidence of post-procedure GERD when compared with conventional POEM. This is an international multicenter randomized controlled trial conducted between high volume expert centers from Hong Kong SAR, China, India and United States of America. Adult patients with manometry confirmed achalasia would be randomised to undergo POEM-F or POEM. The procedure would be performed by experts with vast experience in POEM. The primary outcome is the incidence of post-procedure GERD at 1 year, defined by the updated Lyon consensus. Secondary outcomes include technical and clinical success rates, adverse events, post-POEM endoscopic and manometry findings as well as patients' symptom scores. Sample size calculation Based on existing pilot comparative data on POEM-F and POEM, it is estimated that 84 patients would be required to demonstrate a difference in post-procedure GERD of 47.6% to 18.2%, with 80% power and false positive rate of 0.05, accounting for 10% loss to follow-up. Purpose and potential The current study proposal could demonstrate the superiority of POEM-F over POEM in reducing post-procedural GERD. It would also demonstrate the safety and reproducibility of the technique in expert centers across the globe. It could potentially replace conventional POEM as the preferred minimally invasive endoscopic treatment for achalasia.

Official Title

Per-oral Endoscopic Myotomy With Fundoplication for Achalasia - an International Multicenter Randomized Controlled Trial

Quick Facts

Study Start:2023-12-01
Study Completion:2026-10-31
Study Type:Not specified
Phase:Not Applicable
Enrollment:Not specified
Status:RECRUITING

Study ID

NCT06042127

Participation Criteria

Researchers look for people who fit a certain description, called eligibility criteria. Some examples of these criteria are a person's general health condition or prior treatments.

Ages Eligible for Study:18 Years to 65 Years
Sexes Eligible for Study:ALL
Accepts Healthy Volunteers:No
Standard Ages:ADULT, OLDER_ADULT
Inclusion CriteriaExclusion Criteria
  1. 1. Adult patient (age ≥18 and ≤65 years-old) and with symptomatic achalasia type I or II.
  2. 2. Capability of understanding and complying with the study requirements, including filling the Eckardt Score, GERD-HRQL and RSI questionnaire and signing the informed consent form.
  3. 3. Patients with achalasia type I, II or III who are one of the following:
  4. * Treatment naïve, or
  5. * Failed prior through-the-scope balloon dilation, Savary or pneumatic dilation
  1. 1. Patients unable or unwilling to provide consent.
  2. 2. Previous esophageal or gastric surgery.
  3. 3. Prior achalasia treatment including Heller myotomy, POEM.
  4. 4. Sigmoid achalasia, or significant esophageal dilatation \>6cm in lower esophagus
  5. 5. Disrupted mucosal integrity at the distal esophagus, eg. Ulcer, fibrotic scars etc
  6. 6. Patients with large hiatal hernias (axial length \> 2 cm and Hill grade \>2).
  7. 7. Patients with significant cardiorespiratory comorbidities which may limit their ability to undertake general anesthesia for the procedure, including ASA grade III or above.
  8. 8. Patients with obesity (Body Mass Index (BMI) ≥ 30).
  9. 9. Pregnant women or those planning pregnancy or breastfeeding women.
  10. 10. Uncorrectable coagulopathy defined by international normalized ratio (INR) \> 1.5 or platelet count \< 50000/µl.

Contacts and Locations

Study Contact

Hon Chi Yip, FRCSEd
CONTACT
35052627
hcyip@surgery.cuhk.edu.hk

Principal Investigator

Hon Chi Yip, FRCSEd
PRINCIPAL_INVESTIGATOR
Chinese University of Hong Kong

Study Locations (Sites)

Johns Hopkins Hospital
Baltimore, Maryland, 21287
United States

Collaborators and Investigators

Sponsor: Chinese University of Hong Kong

  • Hon Chi Yip, FRCSEd, PRINCIPAL_INVESTIGATOR, Chinese University of Hong Kong

Study Record Dates

These dates track the progress of study record and summary results submissions to ClinicalTrials.gov. Study records and reported results are reviewed by the National Library of Medicine (NLM) to make sure they meet specific quality control standards before being posted on the public website.

Study Registration Dates

Study Start Date2023-12-01
Study Completion Date2026-10-31

Study Record Updates

Study Start Date2023-12-01
Study Completion Date2026-10-31

Terms related to this study

Keywords Provided by Researchers

  • POEM
  • Fundoplication
  • GERD

Additional Relevant MeSH Terms

  • Achalasia