RECRUITING

A Study of BH-30236 in Relapsed/ Refractory Acute Myelogenous Leukemia and Higher Risk Myelodysplastic Syndrome

Study Overview

This clinical trial focuses on testing the efficacy of different digital interventions to promote re-engagement in cancer-related long-term follow-up care for adolescent and young adult (AYA) survivors of childhood cancer.

Description

Study BH-30236-01 is a first-in-human (FIH), Phase 1/1b, open-label, dose escalation and expansion study in participants with relapsed/refractory acute myelogenous leukemia (R/R AML) or higher-risk myelodysplastic syndrome (HR-MDS). Phase 1, Part 1 Dose Escalation - Monotherapy will evaluate the safety, tolerability, pharmacokinetics (PK), pharmacodynamics (PD), and preliminary efficacy of BH-30236 administered orally. Approximately 50 participants may be enrolled in Phase 1, Part 1 Dose Escalation - Monotherapy. Phase 1, Part 2 Dose Escalation - Combination with Venetoclax will evaluate the safety, tolerability, pharmacokinetics (PK), pharmacodynamics (PD), and preliminary efficacy of BH-30236 administered as a combination therapy with venetoclax. Approximately 48 participants may be enrolled in Phase 1, Part 2 Dose Escalation - Combination with Venetoclax. Phase 1b (Dose Expansion) will follow Phase 1 to further understand the relationships among dose, exposure, toxicity, tolerability, and clinical activity. Up to 72 participants may be enrolled in Phase 1b of the study as a monotherapy or in combination with venetoclax.

Official Title

A Phase 1/1b Open-Label, Dose Escalation, First-in- Human Study to Evaluate the Safety, Tolerability, Pharmacokinetics, and Preliminary Anti-leukemic Activity of the Orally Available CDC-Like Kinase (CLK) Inhibitor, BH-30236, in Adults With Relapsed or Refractory Acute Myelogenous Leukemia (R/R AML) or Higher-Risk Myelodysplastic Syndrome (HR-MDS)

Quick Facts

Study Start:2024-06-19
Study Completion:2027-06
Study Type:Not specified
Phase:Not Applicable
Enrollment:Not specified
Status:RECRUITING

Study ID

NCT06501196

Participation Criteria

Researchers look for people who fit a certain description, called eligibility criteria. Some examples of these criteria are a person's general health condition or prior treatments.

Ages Eligible for Study:18 Years
Sexes Eligible for Study:ALL
Accepts Healthy Volunteers:No
Standard Ages:ADULT, OLDER_ADULT
Inclusion CriteriaExclusion Criteria
  1. * ≥18 years.
  2. * Diagnosis of relapsed/refractory acute myelogenous leukemia (R/R) AML or higher-risk myelodysplastic syndrome (HR-MDS) with ≥5% bone marrow blast at time of inclusion.
  3. * Prior treatment history must include 1-5 prior lines of therapy.
  4. * ECOG performance status ≤2.
  5. * Adequate organ function evidenced by the following laboratory values:
  6. * Hepatic: Transaminase levels aspartate aminotransferase \[AST\]/ alanine transaminase \[ALT\] ≤ 2.5 × upper limit of normal (ULN). In cases of liver involvement by AML or MDS, AST and ALT \< 5.0 × ULN is acceptable. Total bilirubin ≤ 1.5 × ULN in the absence of documented Gilbert's disease.
  7. * Renal: Measured or calculated creatinine clearance ≥ 60 mL/min (Cockcroft-Gault formula)
  1. * Diagnosis of acute promyelocytic leukemia or chronic myeloid leukemia with blast crisis.
  2. * Prior allogeneic HSCT within 3 months or donor lymphocyte infusion within 30 days of start of therapy;
  3. * Active and uncontrolled infections.
  4. * Unresolved AEs greater than Grade from prior therapies.
  5. * History of other active malignancy (with certain exceptions)
  6. * Prior treatment with a CLK inhibitor.
  7. * Any acute or chronic graft versus host disease requiring systemic therapy within 4 weeks prior to study drug administration with the exception of topical steroids or the equivalent of 20 mg of prednisone or less.

Contacts and Locations

Study Contact

Sponsor Contact
CONTACT
(858) 732-3880
clinicaltrials@bhtherapeutics.com

Principal Investigator

Sponsor Contact
STUDY_DIRECTOR
BlossomHill Therapeutics, Inc.

Study Locations (Sites)

City of Hope Medical Center
Duarte, California, 91010
United States
University of California Los Angeles
Los Angeles, California, 90095
United States
Stanford Cancer Center
Palo Alto, California, 94304
United States
Sylvester Comprehensive Cancer Center
Miami, Florida, 33136
United States
Moffitt Cancer Center
Tampa, Florida, 33612
United States
Northwestern Medicine - Northwestern Memorial Hospital Galter Pavilion
Chicago, Illinois, 60611
United States
Roswell Park Cancer Institute
Buffalo, New York, 14263
United States
Memorial Sloan Kettering Cancer Center
New York, New York, 10065
United States
The Ohio State University Wexner Medical Center - James Cancer Hosp
Columbus, Ohio, 43210
United States
Sarah Cannon Research Institute
Nashville, Tennessee, 37203
United States
The University of Texas M.D. Anderson Cancer Center
Houston, Texas, 77030
United States
Fred Hutchinson Cancer Center
Seattle, Washington, 98109
United States
University of Wisconsin Clinical Science Center
Madison, Wisconsin, 53792
United States

Collaborators and Investigators

Sponsor: BlossomHill Therapeutics

  • Sponsor Contact, STUDY_DIRECTOR, BlossomHill Therapeutics, Inc.

Study Record Dates

These dates track the progress of study record and summary results submissions to ClinicalTrials.gov. Study records and reported results are reviewed by the National Library of Medicine (NLM) to make sure they meet specific quality control standards before being posted on the public website.

Study Registration Dates

Study Start Date2024-06-19
Study Completion Date2027-06

Study Record Updates

Study Start Date2024-06-19
Study Completion Date2027-06

Terms related to this study

Additional Relevant MeSH Terms

  • Leukemia
  • Leukemia, Myeloid
  • Leukemia, Myeloid, Acute
  • Preleukemia
  • Myelodysplastic Syndromes
  • Refractory Acute Myeloid Leukemia