RECRUITING

A Study of ORX750 in Participants With Narcolepsy and Idiopathic Hypersomnia

Study Overview

This clinical trial focuses on testing the efficacy of different digital interventions to promote re-engagement in cancer-related long-term follow-up care for adolescent and young adult (AYA) survivors of childhood cancer.

Description

Narcolepsy Type 1 (NT1), Narcolepsy Type 2 (NT2), and Idiopathic Hypersomnia (IH) are rare conditions that make people feel very sleepy during the day (often referred to as excessive daytime sleepiness \[EDS\]). People living with these conditions might find it hard to stay alert and pay attention when they are at school, working, driving, or performing other daily activities. While all conditions result in feeling sleepy, there are some differences in other common symptoms: * NT1: People with NT1 often feel very tired during the day and experience cataplexy. Cataplexy is a sudden loss of muscle strength, which can cause someone to collapse or lose control of their muscles for a short time. This is often triggered by strong emotions, such as laughter or surprise. They may also have trouble sleeping well at night. * NT2: People with NT2 feel sleepy during the day, just like NT1, but they do not have cataplexy. * IH: People with IH feel tired during the day, even after sleeping a lot at night. They may sleep for long periods, take long naps, and find it hard to wake up. Orexin is a protein in the brain that helps coordinate a system that plays an important role in helping people to stay awake during the daytime. ORX750 is designed to mimic the action of orexin. The purpose of this study is to see how safe and tolerable ORX750 is in NT1, NT2, and IH, and learn about what the drug does to the body. Another goal of the study is to see if ORX750 can help people with NT1, NT2, and IH feel less sleepy and make other symptoms better.

Official Title

A Phase 2a, Randomized, Double-blind, Placebo-controlled Study of the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of ORX750 in Subjects With Narcolepsy and Idiopathic Hypersomnia (CRYSTAL-1)

Quick Facts

Study Start:2024-12-23
Study Completion:2025-12
Study Type:Not specified
Phase:Not Applicable
Enrollment:Not specified
Status:RECRUITING

Study ID

NCT06752668

Participation Criteria

Researchers look for people who fit a certain description, called eligibility criteria. Some examples of these criteria are a person's general health condition or prior treatments.

Ages Eligible for Study:18 Years to 65 Years
Sexes Eligible for Study:ALL
Accepts Healthy Volunteers:No
Standard Ages:ADULT, OLDER_ADULT
Inclusion CriteriaExclusion Criteria
  1. * 18-65 years of age
  2. * BMI ≥17 and ≤37 kg/m2
  3. * Meets the diagnostic criteria of Narcolepsy Type 1 (NT1), Type 2 (NT2) or Idiopathic Hypersomnia (IH) according to ICSD-3-TR criteria
  4. * Is willing and able to discontinue all medications used for the treatment of narcolepsy or idiopathic hypersomnia
  5. * Is willing and able to adhere to additional protocol requirements
  1. * A medical disorder other than NT1, NT2, or IH that is associated with excessive daytime sleepiness (EDS).
  2. * Presence of significant cardiovascular, pulmonary, gastrointestinal, hepatic, renal, hematological, malignancy, endocrine, neurological or psychiatric disease

Contacts and Locations

Study Contact

Centessa Pharmaceuticals
CONTACT
+1 617-468-5770
CRYSTAL-1@centessa.com

Study Locations (Sites)

Chandler, Arizona
Chandler, Arizona, 85224
United States
Scottsdale, AZ
Scottsdale, Arizona, 85255
United States
Miami, Florida
Miami, Florida, 33176
United States
Winter Park, Florida
Winter Park, Florida, 32789
United States
Atlanta, Georgia
Atlanta, Georgia, 30328
United States
Henderson, Nevada
Henderson, Nevada, 89052
United States
Denver, North Carolina
Denver, North Carolina, 28037
United States
Huntersville, North Carolina
Huntersville, North Carolina, 28078
United States
Cincinnati, Ohio
Cincinnati, Ohio, 45235
United States
Columbia, South Carolina
Columbia, South Carolina, 29201
United States
San Antonio, Texas
San Antonio, Texas, 78229
United States

Collaborators and Investigators

Sponsor: Centessa Pharmaceuticals (UK) Limited

Study Record Dates

These dates track the progress of study record and summary results submissions to ClinicalTrials.gov. Study records and reported results are reviewed by the National Library of Medicine (NLM) to make sure they meet specific quality control standards before being posted on the public website.

Study Registration Dates

Study Start Date2024-12-23
Study Completion Date2025-12

Study Record Updates

Study Start Date2024-12-23
Study Completion Date2025-12

Terms related to this study

Additional Relevant MeSH Terms

  • Narcolepsy Type 1
  • Narcolepsy Type 2
  • Idiopathic Hypersomnia