RECRUITING

A Study of the Blood Levels of Palovarotene in Participants With Abnormal Liver Function Compared to Healthy Adult Participants After Intake of a Single Dose

Study Overview

This clinical trial focuses on testing the efficacy of different digital interventions to promote re-engagement in cancer-related long-term follow-up care for adolescent and young adult (AYA) survivors of childhood cancer.

Description

The main aim of this study is to understand how moderate and severe liver impairment (based on the Child-Pugh classification) affects the body's processing of a single dose of 10 mg maximum of palovarotene, compared to healthy participants with normal liver function. The study will also assess the safety and tolerability of the single dose of palovarotene. Participants will be enrolled in stages and divided into three groups based on their liver function: * Group 1: Healthy participants with normal liver function * Group 2: Participants with moderate liver impairment * Group 3: Participants with severe liver impairment (only enrolled if Group 2 results are safe and acceptable) Blood samples will be taken to assess how the drug binds to proteins in the blood. Participants will undergo various safety checks and procedures. Participants will stay in the clinical unit until Day 5 for these assessments and will return on Day 10 for a final visit.

Official Title

A Phase I, Open-label, Parallel-group Study to Evaluate the Single-dose Pharmacokinetics of Palovarotene in Male and Female Participants With Moderate and Severe Hepatic Impairment and Matched Participants With Normal Hepatic Function

Quick Facts

Study Start:2025-03-14
Study Completion:2026-06-17
Study Type:Not specified
Phase:Not Applicable
Enrollment:Not specified
Status:RECRUITING

Study ID

NCT06908954

Participation Criteria

Researchers look for people who fit a certain description, called eligibility criteria. Some examples of these criteria are a person's general health condition or prior treatments.

Ages Eligible for Study:18 Years to 70 Years
Sexes Eligible for Study:ALL
Accepts Healthy Volunteers:Yes
Standard Ages:ADULT, OLDER_ADULT
Inclusion CriteriaExclusion Criteria
  1. * Male and female participants must be 18 to 70 years of age (inclusive) at the time of signing informed consent.
  2. * Body weight at least 60.0 kg with body mass index (BMI) within the range of 18.0 and 36.0 kg/m² (inclusive), at screening. BMI of \>36.0 to ≤37.0 may be eligible if participant has ascites scoring 3 points on the C-P criteria.
  3. * Contraceptive use by men or women should be consistent with local regulations regarding the methods of contraception for those participating in clinical trials
  4. * Clinical diagnosis of chronic hepatic disease (stable for more than 3 months) with a documented history of underlying hepatic insufficiency and no acute episodes of illness within 30 days prior to Day -1 (admission) and no significant change in disease status (i.e. up to 1 point in the C-P classification) from screening to Day -1.
  5. * A stable medication regimen, defined as not starting new therapy(ies) or significant changing dosage(s) within 30 days prior to dosing.
  1. * Presence or significant history of cardiovascular, respiratory, hepatic (except for the hepatic impairment for those concerned), renal, gastrointestinal, biliary, mucocutaneous, endocrinological, haematological or neurological disorders capable of significantly altering the absorption, metabolism, or elimination of drugs, constituting a risk when taking the study intervention, or interfering with the interpretation of data.
  2. * Lymphoma, leukaemia or any malignancy within the past 5 years except for basal cell or squamous epithelial carcinomas of the skin that have been resected with no evidence of metastatic disease for 3 years.
  3. * Breast cancer within the past 10 years.
  4. * Use of any medications (prescription or over the counter), herbal tea, energy drinks (including natural stimulants), herbal products (e.g. St. John's wort, garlic, milk thistle) or supplements/supratherapeutic doses of vitamins within 14 days prior to Day 1 and through discharge, apart from those approved by the investigator and the sponsor's medical monitor. Those with hepatic impairment may take concomitant medications
  5. * Use of any medications that are moderate or strong inhibitors or inducers of CYP3A4
  6. * Donation or loss (excluding volume drawn at screening or during menses) of more than 250 mL of blood or blood product within 3 months prior to screening. In addition, plan of blood donation within 8 weeks after the last PK sampling.
  7. * Presence of hepatitis B surface antigen (HBsAg) at screening or within 3 months prior to the dose of study intervention.
  8. * Positive hepatitis C antibody test result at screening or within 3 months prior to the dose of study intervention. Note: Participants with positive hepatitis C antibody due to prior resolved disease can be enrolled if a confirmatory negative hepatitis C ribonucleic acid (RNA) test is obtained.
  9. * Positive hepatitis C RNA test result at screening or within 3 months prior to the dose of study intervention. Note: Test is optional and participants with negative hepatitis C antibody test are not required to also undergo hepatitis C RNA testing.
  10. * Sensitivity to the study intervention, or components thereof (including inactive ingredients), or drug or other allergy that, in the opinion of the investigator (or medical monitor), contraindicates participation in the study
  11. * Evidence of relevant active disease at screening, including gastroenterological (other than hepatic cirrhosis), cardiac (e.g. myocardial infarction in the past year, angina or congestive heart failure), renal, respiratory, haematological, neuropsychiatric or neoplastic (basal or squamous cell skin cancer is acceptable) disease.
  12. * Acute hepatitis B (positive for HBsAg) or acute hepatitis C (positive for anti-hepatitis C virus (HCV) for a duration of less than 6 months). Note: Participants with chronic HCV (positive for HCV RNA or anti-HCV for more than 6 months) are eligible for enrolment, if stable, as assessed by the investigator.
  13. * Primary sclerosing cholangitis or preliminary diagnosed biliary obstruction at screening.
  14. * Current or chronic history of liver disease. This includes (but is not limited to hepatitis virus infections), drug- or alcohol-related liver disease, non-alcoholic steatohepatitis, autoimmune hepatitis, hemochromatosis, Wilson's disease, α-1 antitrypsin deficiency, primary biliary cholangitis, primary sclerosing cholangitis, or any other liver disease considered clinically significant by the investigator.

Contacts and Locations

Study Contact

Ipsen Clinical Study Enquiries
CONTACT
See e mail
clinical.trials@ipsen.com

Principal Investigator

Ipsen Medical Director
STUDY_DIRECTOR
Ipsen

Study Locations (Sites)

Central Research Associates
Birmingham, Alabama, 35205
United States
CCT Research
Phoenix, Arizona, 85044
United States
HonorHealth Neurology
Scottsdale, Arizona, 85251
United States
Alliance for Multispecialty Research (AMR) Phoenix
Tempe, Arizona, 85281
United States
Fullerton Neurological Center
Fullerton, California, 92835
United States
Neurology Center of North Orange County
Fullerton, California, 92835
United States
Neurological Research Institute of Southern California
Los Angeles, California, 90067
United States
SDS Clinical Trials
Orange, California, 92868
United States
Visionary Investigators Network (VIN)
Aventura, Florida, 33180
United States
AGA Clinical Trials
Hialeah, Florida, 33012
United States
University of Miami Leonard M. Miller School of Medicine - Professional Arts Center
Miami, Florida, 33136
United States
ERG - Clinical Pharmacology of Miami
Miami, Florida, 33172
United States
Orlando Clinical Research Center
Orlando, Florida, 32809
United States
Conquest Research
Winter Park, Florida, 32789
United States
MD Fort Wayne Neurological Center
Fort Wayne, Indiana, 46804
United States
Comprehensive Neurology Services
Frederick, Maryland, 21702
United States
Boston Clinical Trials Inc
Boston, Massachusetts, 02131
United States
New England Regional Headache Center, Inc.
Worcester, Massachusetts, 01609
United States
Quest Research Institute
Farmington Hills, Michigan, 48334
United States
Minneapolis Clinic of Neurology
Burnsville, Minnesota, 55337
United States
SPRI Clinical Trials, LLC
Brooklyn, New York, 11235
United States
Nuvance Health Medical Practice
Poughkeepsie, New York, 12601
United States
Rochester Clinical Research, Inc
Rochester, New York, 14609
United States
Asheville Neurology Specialists
Asheville, North Carolina, 28806
United States
Headache Wellness Center
Greensboro, North Carolina, 27405
United States
OrthoNeuro
New Albany, Ohio, 43054
United States
Suburban Research Associates
Media, Pennsylvania, 19063
United States
Thomas Jefferson University Hospital - Jefferson Hospital for Neuroscience - Jefferson Neurology Associates - Neurology
Philadelphia, Pennsylvania, 19107
United States
Coastal Carolina Research Center - North Charleston
North Charleston, South Carolina, 29405
United States
Neurology Clinic, PC
Cordova, Tennessee, 38018
United States
Texas Neurology
Dallas, Texas, 75214
United States
Research Your Health
Plano, Texas, 75093
United States
American Research Corporation/Texas Liver Institute
San Antonio, Texas, 78215
United States
J. Lewis Research Inc.-Foothill Family Clinic
Salt Lake City, Utah, 84109
United States
Metrodora Institute
West Valley City, Utah, 84119
United States
Inova Medical Group - Neurology
Fairfax, Virginia, 22031
United States
MedStar Health - Department of Neurology
Columbia, Washington, 20010
United States
Frontier Clinical Research, LLC
Kingwood, West Virginia, 26537
United States

Collaborators and Investigators

Sponsor: Ipsen

  • Ipsen Medical Director, STUDY_DIRECTOR, Ipsen

Study Record Dates

These dates track the progress of study record and summary results submissions to ClinicalTrials.gov. Study records and reported results are reviewed by the National Library of Medicine (NLM) to make sure they meet specific quality control standards before being posted on the public website.

Study Registration Dates

Study Start Date2025-03-14
Study Completion Date2026-06-17

Study Record Updates

Study Start Date2025-03-14
Study Completion Date2026-06-17

Terms related to this study

Additional Relevant MeSH Terms

  • Hepatic Impairment
  • Healthy